Renewed Hope: Novel Treatments for Spinal Muscular Atrophy Improving Outcomes


Spinal muscular atrophy (SMA) is a rare autosomal recessive neuromuscular disease that presents as progressive muscle weakness secondary to loss of lower motor neurons in the brainstem and spinal cord. With an incidence of 1 in 10,000 live births, SMA is the most common genetic cause of death in infancy, but new treatments may soon … Continue reading Renewed Hope: Novel Treatments for Spinal Muscular Atrophy Improving Outcomes